From Blindness to Functional Sight in One Shot
“Children who were treated with gene therapy are now able to walk and play just like any normally sighted child,” said co-first author Albert M. Maguire, M.D., an associate professor of Ophthalmology at Penn and a physician at Children’s Hospital. “They can also carry out classroom activities without visual aids.”
The doctors use a virus as a vector to introduce the new genes into the patient’s retinas. Simply amazing.
